Personalized gene therapy relieves severe epilepsy in two boys
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Targeting neurons (artist’s illustration) that had an abnormal flow of sodium ions reduced epileptic seizures in two people. Credit: Kateryna Kon/SPL
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A tailored treatment has reduced seizures and improved developmental skills in two boys with debilitating neurological disorders1.
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doi: https://doi.org/10.1038/d41586-026-02267-0
References<br>Kim-McManus, O. et al. Nature Med. https://doi.org/10.1038/s41591-026-04527-y (2026).<br>Article<br>PubMed
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